We are testing a new medication called GHF-201 in healthy adults to see how safe it is and how the body handles it. This study aims to gather important information before it can be used in patients.
Health conditions and diseases that the clinical trial is designed to study and treat.
Adult Polyglucosan Body Disease (APBD) is a rare genetic disorder characterized by the accumulation of abnormal glycogen in the body, leading to neurological symptoms such as muscle weakness, difficulty walking, and cognitive decline.
Locations and medical facilities where this clinical trial is currently recruiting or conducting research. Select the locations where you would like to participate.
Disclaimer: Parts of this content have been automatically extracted from the EU Clinical Trials registry. While we strive for accuracy, please always contact the trial site or sponsor directly for correct and official information before making any decisions about participation. View on EU Clinical Trials.